Profiling tofersen as a treatment of superoxide dismutase 1 amyotrophic lateral sclerosis
Miguel Oliveira Santos; Mamede de Carvalho · 2024 · Expert Review of Neurotherapeutics
WASTE classifies this as Failed Experiment Report · AI classification, approximate
An experimental approach did not work as intended — learn what to avoid before investing the same effort.
Abstract (excerpt)
INTRODUCTION: Amyotrophic lateral sclerosis (ALS) is a rapidly progressive motor neuron disorder with a fatal outcome 3-5 years after disease onset due to respiratory complications. Superoxide dismutase 1 (SOD1) mutations are found in…
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Metadata source: OpenAlex · DOI 10.1080/14737175.2024.2355983